University of Alberta Medical Genetics Clinic
Edmonton, Alberta T6G 2B7
2 studies enrolling now · 2 studies all time
What they study most
GM1 Gangliosidosis, GM2 Gangliosidosis, Niemann-Pick Type C Disease
Studies at this site
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis — Recruiting now
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC) — Recruiting now