UCL Great Ormond Street Institute of Child Health

London WC1N 1EH

2 studies enrolling now · 5 studies all time

What they study most

Adenosine Deaminase Deficiency, Advanced Solid Tumor, Epilepsy, GM1 Gangliosidosis, Hypothalamic Obesity, Low-grade Glioma, Severe Combined Immunodeficiency (SCID)

Studies at this site

• A Study to Evaluate Tovorafenib in Pediatric and Young Adult Participants With Relapsed or Progressive Low-Grade Glioma and Advance Solid Tumors — Recruiting now
• A Trial of Setmelanotide in Acquired Hypothalamic Obesity — Running, not enrolling
• An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID — Enrolling by invitation
• Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients — Completed
• Gene-STEPS: Shortening Time of Evaluation in Paediatric Epilepsy Services — Status unconfirmed