The Lysosomal & Rare Disorders Research & Treatment Center

Fairfax, Virginia 22030

1 studies enrolling now · 1 studies all time

What they study most

Late-onset Pompe Disease

Studies at this site

• A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease — Recruiting now