The Children's Hospital of Philadelphia - Hematology

Philadelphia, Pennsylvania 19104

1 studies enrolling now · 2 studies all time

What they study most

Beta-Thalassemia, Genetic Diseases, Inborn, Hematologic Diseases, Hematological Diseases, Hemoglobinopathies, Hydroxyurea Failure, Hydroxyurea Intolerance, Sickle Cell Anemia, Sickle Cell Disease, Thalassemia

Studies at this site

• Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD) — Running, not enrolling
• A Long-term Follow-up Study in Participants Who Received CTX001 — Enrolling by invitation