Texas Childrens Hospital Houston

Houston, Texas 77030

3 studies enrolling now · 5 studies all time

What they study most

Congenital Bleeding Disorder, Congenital Haemophilia, Haemophilia A and B With and Without Inhibitors, Haemophilia B, Muscular Atrophy, Spinal, Sickle Cell Disease, Thalassemia

Studies at this site

• A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia — Recruiting now
• A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK) — Recruiting now
• A Research Study on How Well Concizumab Works for You if You Have Haemophilia A or B With or Without Inhibitors — Running, not enrolling
• Compassionate Use of Concizumab if You Have Haemophilia — Available (expanded access)
• Safety, Efficacy and Pharmacokinetics of NNC-0156-0000-0009 in Previously Treated Children With Haemophilia B. — Completed