Rare Disease Research

Iselin, New Jersey 08830

1 studies enrolling now · 1 studies all time

What they study most

Genetic Diseases, Inborn, Genetic Diseases, X-Linked, Muscular Diseases, Muscular Disorders, Atrophic, Muscular Dystrophies, Muscular Dystrophy, Duchenne, Musculoskeletal Diseases, Nervous System Diseases, Neuromuscular Diseases

Studies at this site

• Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 Skipping — Available (expanded access)