Osp. Pediatrico Bambino Gesù, IRCCS

Rome

1 studies enrolling now · 2 studies all time

What they study most

Mucopolysaccharidosis II

Studies at this site

• A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT) — Running, not enrolling
• An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in MPS II (Hunter Syndrome) Subjects — Enrolling by invitation