Ospedale Pediatrico Bambino Gesù IRCCS
Roma
2 studies enrolling now · 3 studies all time
What they study most
CLOVES Syndrome, Cystic Fibrosis, Klippel Trenaunay Syndrome, Lymphatic Malformations, Megalencephaly-capillary Malformation Polymicrogyria Syndrome (MCAP), PIK3CA Mutation, PIK3CA-Related Overgrowth Spectrum (PROS), Prader-Willi Syndrome, Vascular Anomalies, Vascular Malformations
Studies at this site
- A Phase 2 Study of Mutant-selective PI3Kα Inhibitor, RLY-2608, in Adults and Children With PIK3CA Related Overgrowth Spectrum and Malformations Driven by PIK3CA Mutation (The ReInspire Study) — Recruiting now
- A Study of Pitolisant in Patients With Prader-Willi Syndrome — Recruiting now
- Study of Ataluren in Nonsense Mutation Cystic Fibrosis (ACT CF) — Completed