Lysosomal Rare Disorders Research & Treatment Center

Fairfax, Virginia 22030-7404

0 studies enrolling now · 6 studies all time

What they study most

Fabry Disease, Gaucher Disease, Humoral Immune Response, Primary Immune Deficiency Disorder, Rhinoconjunctivitis, Seasonal Allergic Rhinitis

Studies at this site

• Safety, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged >12 Years) With Fabry Disease — Completed
• Efficacy and Safety of PQ Grass in Subjects With Seasonal Allergic Rhinitis and/or Rhinoconjunctivitis Induced by Grass Pollen — Completed
• A Study of Velaglucerase Alfa (VPRIV) Given as Standard Patient Care in Young Children With Gaucher Disease — Completed
• Assess Urine Biomarkers to Predict Nephropathy in Fabry Disease — Status unconfirmed
• A Study About Low Blood Pressure in Patients With Primary Immunodeficiency Disease Treated With Immune Globulin Products — Status unconfirmed
• Study to Evaluate Safety and Pharmacokinetics of BIVIGAM® in Primary Immune Deficiency Subjects Aged 2 to 16 — Completed