Lysosomal and Rare Disorders Research & Treatment Center
Fairfax, Virginia 22030
0 studies enrolling now ยท 1 studies all time
What they study most
Acid Maltase Deficiency, Glycogen Storage Disease Type 2, Glycogen Storage Disease Type II, LOPD, Lysosomal Storage Diseases, Pompe Disease, Pompe Disease (Late-onset)
Studies at this site
- A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE) โ Running, not enrolling