JK Lone Hospital
Jaipur, Rajasthan 302004
2 studies enrolling now · 3 studies all time
What they study most
GM1 Gangliosidosis, GM2 Gangliosidosis, Gangliosidoses, GM2, Gangliosidosis, GM1, Niemann-Pick Type C Disease
Studies at this site
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis — Recruiting now
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC) — Recruiting now
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis — Running, not enrolling