IRCSS Ospedale Pediatrico Bambino Gesu - Dipartimento di Onco-Ematologia e Terapia Cellulare e Genica

Rome

2 studies enrolling now · 4 studies all time

What they study most

Beta-Thalassemia, Genetic Diseases, Inborn, Hematologic Diseases, Hematological Diseases, Hemoglobinopathies, Hydroxyurea Failure, Hydroxyurea Intolerance, Sickle Cell Anemia, Sickle Cell Disease, Thalassemia

Studies at this site

• Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease — Recruiting now
• Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD) — Running, not enrolling
• Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT) — Running, not enrolling
• A Long-term Follow-up Study in Participants Who Received CTX001 — Enrolling by invitation