IRCCS Istituto Giannina Gaslini

Genoa 16147

0 studies enrolling now · 3 studies all time

What they study most

ASAH1 Mutation, Acid Ceramidase Deficiency, Anti-myostatin, Atrophy, Ceramidase Deficiency, Farber Disease, Farber Lipogranulomatosis, Farber's Disease, Fibrodysplasia Ossificans Progressiva, Muscular Atrophy, Muscular Atrophy, Spinal, N-Laurylsphingosine Deacylase Deficiency

Studies at this site

• A Study to Assess Safety, Tolerability and Efficacy of Garetosmab Versus Placebo Administered Intravenously (IV) in Adult Participants With Fibrodysplasia Ossificans Progressiva (FOP) — Running, not enrolling
• Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam — Completed
• Farber Disease Natural History Study — Completed