Ionis Investigative Site

Philadelphia, Pennsylvania 19107-5109

2 studies enrolling now · 7 studies all time

What they study most

Age Related Macular Degeneration, Familial Chylomicronemia Syndrome, Familial Partial Lipodystrophy, Geographic Atrophy, Hyperlipoproteinemia Type 1, Lipoprotein Lipase Deficiency, Macular Degeneration, Pelizaeus-Merzbacher Disease

Studies at this site

• Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease — Recruiting now
• Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD) — Recruiting now
• GOLDEN STUDY: A Study to Assess Safety and Efficacy of Multiple Doses of IONIS-FB-LRx in Participants With Geographic Atrophy Secondary to Age-Related Macular Degeneration (AMD) — Completed
• The APPROACH Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Patients With Familial Chylomicronemia Syndrome — Completed
• The BROADEN Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Participants With Familial Partial Lipodystrophy — Stopped early
• The Approach Open Label Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Participants With Familial Chylomicronemia Syndrome — Completed
• Safety and Efficacy of IONIS-FB-Lrx in up to 120 Patients 55 and Older With Geographic Atrophy (GA) Secondary to Age-Related Macular Degeneration (AMD) — Withdrawn before enrolling