Investigational Site Number : 250002

Bron 69677

1 studies enrolling now · 4 studies all time

What they study most

Fabry Disease, Sphingomyelin Lipidosis

Studies at this site

• Fabry Disease Registry & Pregnancy Sub-registry — Recruiting now
• A Long-Term Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency — Completed
• Safety, Tolerability, PK, and Efficacy Evaluation of Repeat Ascending Doses of Olipudase Alfa in Pediatric Patients <18 Years of Age With Acid Sphingomyelinase Deficiency — Completed
• A Study of Renal Function in Treatment-naïve, Young Male Patients With Fabry Disease — Stopped early