Investigational Site Number : 2500001

Tours 37044

0 studies enrolling now · 2 studies all time

What they study most

Glycogen Storage Disease Type II, Glycogen Storage Disease Type II-Pompe's Disease

Studies at this site

• A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD) — Running, not enrolling
• A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa — Running, not enrolling