Instytut Matki i Dziecka

Warsaw 01-211

4 studies enrolling now · 11 studies all time

What they study most

Advanced Solid Tumor, Cystic Fibrosis, Giant Cell Tumor of Bone, Homocystinuria, Osteosarcoma, Osteosarcoma in Adolescents and Young Adults, Osteosarcoma in Children, PMM2-CDG, Phenylketonuria, Phosphomannomutase 2 Deficiency, Pseudomonas Aeruginosa, Thrombocytopenia, Neonatal Alloimmune

Studies at this site

• A Study to Investigate Efficacy and Safety of Pegtibatinase Compared With Placebo in Participants ≥12 to ≤65 Years of Age With Classical Homocystinuria (HCU) Due to Cystathionine Beta Synthase Deficiency Receiving Standard of Care Treatment — Recruiting now
• A Study of Sepiapterin in Participants With Phenylketonuria (PKU) — Recruiting now
• A Study of Nipocalimab or Intravenous Immunoglobulin (IVIG) in Pregnancies At Risk of Fetal and Neonatal Alloimmune Thrombocytopenia (FNAIT) — Recruiting now
• A Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE) — Enrolling by invitation
• A Study of Erdafitinib in Participants With Advanced Solid Tumors and Fibroblast Growth Factor Receptor (FGFR) Gene Alterations — Completed
• Effects of Maintenance Cabozantinib+BSC Versus BSC in Children and AYA With Osteosarcoma — Stopped early
• A Study to Assess the Efficacy and Safety of Weekly Doses of GLM101 in Participants With PMM2-CDG — Running, not enrolling
• Long-term Safety Follow-up of Subjects With Giant Cell Tumor of Bone Treated With Denosumab in Study 20062004 — Completed
• Study of Ataluren in Nonsense Mutation Cystic Fibrosis (ACT CF) — Completed
• A Phase 3 Study of VX-659 Combination Therapy in Subjects With Cystic Fibrosis Heterozygous for the F508del Mutation and a Minimal Function Mutation (F/MF) — Completed
• Safety of AZLI in Children With Cystic Fibrosis (CF) and Chronic Pseudomonas Aeruginosa in the Lower Airways — Completed