Instituto de Puericultura E Pediatria Martagão Gesteira
Rio de Janeiro, Rio de Janeiro CEP 21941-912
0 studies enrolling now · 3 studies all time
What they study most
Juvenile Idiopathic Arthritis, Muscular Atrophy, Spinal
Studies at this site
- Investigate Safety, Tolerability, PK, PD and Efficacy of Risdiplam (RO7034067) in Infants With Type1 Spinal Muscular Atrophy — Completed
- A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants — Completed
- A Study of Tocilizumab in Patients With Active Polyarticular Juvenile Idiopathic Arthritis — Completed