Instituto de Genética e Erros Inatos do Metabolismo
São Paulo
1 studies enrolling now · 2 studies all time
What they study most
Mucopolysaccharidosis II
Studies at this site
- A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT) — Running, not enrolling
- An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in MPS II (Hunter Syndrome) Subjects — Enrolling by invitation