Hôpital Universitaire des Enfants Reine Fabiola

Brussels 1020

2 studies enrolling now · 8 studies all time

What they study most

Chronic Graft-versus-host-disease, Cystic Fibrosis, Haemophilia A, Limb-girdle Muscular Dystrophy, Ulcerative Colitis

Studies at this site

• A Study to Evaluate Axatilimab Versus Best Available Therapy in Pediatric Participants With Chronic Graft-Versus-Host Disease After at Least 2 Prior Lines of Systemic Therapy (AGAVE-256) — Recruiting now
• Efficacy, Safety & Utilisation of Nuwiq, Octanate and Wilate in Previously Untreated & Minimally Treated Haemophilia A Patients — Recruiting now
• Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative Colitis — Running, not enrolling
• A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice — Running, not enrolling
• Extension Study of Ataluren (PTC124) in Cystic Fibrosis — Completed
• Study of Ataluren in Nonsense Mutation Cystic Fibrosis (ACT CF) — Completed
• Study of Ataluren (PTC124™) in Cystic Fibrosis — Completed
• Study of Ataluren (PTC124) in Cystic Fibrosis — Stopped early