Hôpital Necker-Enfants Malades; Service de neuropédiatrie

Paris 75015

0 studies enrolling now · 1 studies all time

What they study most

Muscular Atrophy, Spinal

Studies at this site

• A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants — Completed