Hôpital Necker - Enfants Malades

Paris, Paris 75743

2 studies enrolling now · 8 studies all time

What they study most

Invasive Aspergillosis, Invasive Fungal Infections, Methylmalonic Acidemia, Propionic Acidemia, Thrombotic Thrombocytopenic Purpura (TTP), Von Willebrand Disease (VWD), X-Linked Hypohidrotic Ectodermal Dysplasia (XLHED)

Studies at this site

• A Retrospective Study to Characterize Participants With Propionic Acidemia — Recruiting now
• Intraamniotic Administrations of ER004 to Male Subjects With X-linked Hypohidrotic Ectodermal Dysplasia — Recruiting now
• A Study of TAK-755 in Participants With Congenital Thrombotic Thrombocytopenic Purpura — Running, not enrolling
• A Study of BAX 930 in Children, Teenagers, and Adults Born With Thrombotic Thrombocytopenic Purpura (TTP) — Completed
• Olorofim Aspergillus Infection Study — Running, not enrolling
• A Study of Recombinant Von Willebrand Factor (rVWF) in Pediatric and Adult Participants With Severe Von Willebrand Disease (VWD) — Completed
• Evaluate F901318 (Olorofim) Treatment of Invasive Fungal Infections in Participants Lacking Treatment Options — Completed
• "The MaP Study": Mapping the Patient Journey in MMA and PA — Completed