Hôpital Femme-Mère-Enfant

Bron 69677

3 studies enrolling now · 9 studies all time

What they study most

Biliary Atresia, Cystic Fibrosis, Hunter Syndrome, Hypochondroplasia, IGF1 Deficiency, Ichthyosis, MPS IVA, Morquio A Syndrome, Mucopolysaccharidosis II, Mucopolysaccharidosis IV Type A, Plaque Psoriasis

Studies at this site

• Global Patient Registry to Monitor Long-term Safety and Effectiveness of Increlex® in Children and Adolescents With Severe Primary Insulin-like Growth Factor-1 Deficiency (SPIGFD). — Recruiting now
• Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD) — Completed
• Open-Label, Long-Term, Extension Study of Infigratinib in Children With Hypochondroplasia — Enrolling by invitation
• The ASCEND Study: Evaluating TMB-001 in the Treatment of RXLI or ARCI Ichthyosis — Completed
• An Extension Study of JR-141 to Evaluate the Long-term Safety and Efficacy in MPS II (Hunter Syndrome) Subjects — Enrolling by invitation
• A Multicenter, Multinational, Observational Morquio A Registry Study (MARS) — Completed
• Study of Ixekizumab (LY2439821) in Children 6 to Less Than 18 Years With Moderate-to-Severe Plaque Psoriasis — Completed
• Study of Intrathecal Idursulfase-IT Administered in Conjunction With Elaprase® in Pediatric Patients With Hunter Syndrome and Early Cognitive Impairment — Completed
• Study of Ataluren in Nonsense Mutation Cystic Fibrosis (ACT CF) — Completed