Hôpital Armand-Trousseau, Centre de Référence des Maladies Lysosomales (CRML), Service de Neuropédiatrie

Paris 75012

0 studies enrolling now · 1 studies all time

What they study most

GM1 Gangliosidosis

Studies at this site

• A Safety and Efficacy Study of LYS-GM101 Gene Therapy in Patients With GM1 Gangliosidosis — Stopped early