Hospital Universitario Vall d'Hebron - PPDS
Barcelona, Barcelona 8035
3 studies enrolling now · 4 studies all time
What they study most
GM1 Gangliosidosis, GM2 Gangliosidosis, Gangliosidoses, GM2, Gangliosidosis, GM1, Niemann-Pick Type C Disease, Non-cystic Fibrosis Bronchiectasis
Studies at this site
- A Phase II Study of Ensifentrine in Non-Cystic Fibrosis Bronchiectasis — Recruiting now
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis — Recruiting now
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC) — Recruiting now
- A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis — Running, not enrolling