Hospital Tunku Azizah
Kuala Lumpur 50300
0 studies enrolling now · 3 studies all time
What they study most
Netherton Syndrome, Non-Transfusion-dependent Alpha-Thalassemia, Non-Transfusion-dependent Beta-Thalassemia, Transfusion-dependent Alpha-Thalassemia, Transfusion-dependent Beta-Thalassemia
Studies at this site
- A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT) — Running, not enrolling
- A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) — Running, not enrolling
- A Study to Test Whether Spesolimab Helps People With a Skin Disease Called Netherton Syndrome — Stopped early