Hospital Pequeno Principe

Curitiba 80250-060

2 studies enrolling now · 5 studies all time

What they study most

Colitis, Ulcerative, GM1 Gangliosidosis, Hypertension, Pulmonary, Niemann-Pick Type C Disease, Sandhoff Disease, Tay-Sachs Disease

Studies at this site

• A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC) — Recruiting now
• A Protocol of Icotrokinra Therapy in Adult and Adolescent Participants With Moderately to Severely Active Ulcerative Colitis — Recruiting now
• A Study of Selexipag as Add-On Treatment to Standard of Care in Children With Pulmonary Arterial Hypertension — Running, not enrolling
• A Study to Assess the Efficacy and Safety of Golimumab in Pediatric Participants With Moderately to Severely Active Ulcerative Colitis — Running, not enrolling
• GM1 and GM2 Gangliosidosis PROspective Neurological Disease TrajectOry Study (PRONTO) — Completed