Hospital Necker-Enfants Malades

Paris 75015

0 studies enrolling now · 3 studies all time

What they study most

Cushing Syndrome, Lysosomal Acid Lipase Deficiency, Pulmonary Arterial Hypertension, Wolman Disease

Studies at this site

• Pharmacokinetic (PK), Pharmacodynamic (PD) and Tolerability of Osilodrostat in Pediatric Patients With Cushing's Syndrome — Recruiting now
• BREATHE 5-OL: Tracleer (Bosentan) in Patients With Pulmonary Arterial Hypertension Related to Eisenmenger Physiology — Completed
• A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype — Completed