Great Ormond Street Hospital NHS Foundation Trust

London WC1N 3JH

1 studies enrolling now · 3 studies all time

What they study most

MPS IVA, Morquio A Syndrome, Mucopolysaccharidosis IV Type A, Pompe Disease, Pulmonary Hypertension, Familial Persistent, of the Newborn

Studies at this site

• A Global Prospective Observational Registry of Patients With Pompe Disease — Recruiting now
• A Multicenter, Multinational, Observational Morquio A Registry Study (MARS) — Completed
• A Study To Evaluate Safety And Efficacy Of IV Sildenafil In The Treatment Of Neonates With Persistent Pulmonary Hypertension Of The Newborn — Completed