Great Ormond Street Hospital for Sick Children

London WC1N3JH

0 studies enrolling now · 3 studies all time

What they study most

Cystic Fibrosis, Fabry Disease, Hunter Syndrome, Mucopolysaccharidosis II (MPS II)

Studies at this site

• A Study to Evaluate the Safety of Long-term Ivacaftor Treatment in Participants With Cystic Fibrosis Who Are Less Than 24 Months of Age at Treatment Initiation and Have an Approved Ivacaftor-Responsive Mutation — Completed
• Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II Patients Receiving Idursulfase — Completed
• A Study of Fabrazyme in Pediatric Patients With Fabry Disease — Completed