Great Ormond Street Hospital for NHS Foundation Trust

London WC1N 3JH

0 studies enrolling now · 1 studies all time

What they study most

Batten Disease, CLN2 Disease, Jansky-Bielschowsky Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2

Studies at this site

• A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease — Completed