Great Ormond Street Hospital for Children

London, London WC1N 3JH

1 studies enrolling now · 1 studies all time

What they study most

Mucopolysaccharidosis II

Studies at this site

• A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II) — Recruiting now