Great Ormond Street Childrens Hospital

London WC1N 3JH

0 studies enrolling now · 2 studies all time

What they study most

Batten Disease, CLN2 Disease, CLN2 Disorder, Jansky-Bielschowsky Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2

Studies at this site

• A Safety, Tolerability, and Efficacy Study of BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Disease — Completed
• An Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease — Completed