C.S. Mott Children's Hospital - Hematology / Oncology
Ann Arbor, Michigan 48109
0 studies enrolling now ยท 1 studies all time
What they study most
Hemophilia A
Studies at this site
Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle"
โ Running, not enrolling