Cincinnati Children's Hospital Medical Center- Site Number : 8400001

Cincinnati, Ohio 45229

0 studies enrolling now · 2 studies all time

What they study most

Glycogen Storage Disease Type II

Studies at this site

• A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD) — Running, not enrolling
• Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa — Running, not enrolling