CHOP Children's Hospital of Philadelphia

Philadelphia, Pennsylvania 19104

1 studies enrolling now · 2 studies all time

What they study most

Methylmalonic Acidemia (MMA), Neuromuscular Diseases, SMA, Spinal Muscular Atrophy

Studies at this site

• A Prospective Study of Pediatric Participants up to 16 Years of Age With Methylmalonic Acidemia (MMA) Due to Mutations in the MMUT Gene — Recruiting now
• A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy — Running, not enrolling