Children's Hospital Philadelphia - Neurology

Philadelphia, Pennsylvania 19104

1 studies enrolling now · 2 studies all time

What they study most

Muscular Atrophy, Spinal, Spinal Muscular Atrophy (SMA)

Studies at this site

• A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy — Recruiting now
• A Study to Learn About the Effect of Nusinersen (BIIB058) Given as Injections to Children With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec (RESPOND) — Completed