Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders

Pittsburgh, Pennsylvania 15224

0 studies enrolling now · 3 studies all time

What they study most

Mucopolysaccharidosis II, Mucopolysaccharidosis Type II (MPS II)

Studies at this site

• CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome) — Running, not enrolling
• Mucopolysaccharidosis Type II Natural History — Completed
• Long-term Follow-Up for RGX-121 — Status unconfirmed