Children's Hospital of Philadelphia - Neurology

Philadelphia, Pennsylvania 19104

0 studies enrolling now · 4 studies all time

What they study most

Friedreich Ataxia, Neuro-Degenerative Disease, Spinal Muscular Atrophy

Studies at this site

• FRDA Investigator Initiated Study (IIS) With Elamipretide — Completed
• FA Clinical Outcome Measures — Running, not enrolling
• A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy — Stopped early
• A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Participants With Later-onset Spinal Muscular Atrophy (SMA) — Completed