Childrens Hospital of Fudan University

Shanghai 201102

3 studies enrolling now · 17 studies all time

What they study most

AOSD, Angiofibroma of Face, Biliary Atresia, Dravet Syndrome, Duchenne Muscular Dystrophy, Epilepsy, Fibrodysplasia Ossificans Progressiva (FOP), Generalized Myasthenia Gravis, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, Hypertension, Pulmonary, Juvenile Psoriatic Arthritis

Studies at this site

• A Study to Evaluate the Drug Levels, Efficacy, and Safety of Deucravacitinib (BMS-986165) in Pediatric Participants With Juvenile Psoriatic Arthritis — Recruiting now
• To Assess the Efficacy, Safety, and Tolerability of INCB000928 in Participants With Fibrodysplasia Ossificans Progressiva — Recruiting now
• A Study of Selexipag as Add-On Treatment to Standard of Care in Children With Pulmonary Arterial Hypertension — Running, not enrolling
• Efficacy, Safety, and Pharmacokinetics of Leuprolide Mesylate in Subjects With Central Precocious Puberty — Completed
• Efficacy and Safety of Odevixibat in Children With Biliary Atresia Who Have Undergone a Kasai HPE (BOLD) — Completed
• An Open-label Extension Study to Evaluate Long-term Efficacy and Safety of Odevixibat in Children With Biliary Atresia — Enrolling by invitation
• Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy — Completed
• Evaluate Efficacy, Safety and Tolerability, PK and PD of Emapalumab in Children and Adults With MAS in Still's or SLE — Completed
• Topical Sirolimus Ointment for Cutaneous Angiofibromas in Subjects With Tuberous Sclerosis Complex — Stopped early
• Evaluation of Maralixibat in Biliary Atresia Response Post-Kasai — Completed
• A Study To Evaluate Efficacy, Safety, Pharmacokinetics, And Pharmacodynamics Of Satralizumab In Patients With Generalized Myasthenia Gravis — Stopped early
• Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53) — Completed
• Investigate Safety, Tolerability, PK, PD and Efficacy of Risdiplam (RO7034067) in Infants With Type1 Spinal Muscular Atrophy — Completed
• A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants — Completed
• Steroid Sensitive Nephrotic Syndrome in Children — Stopped early
• A Study Comparing LY900014 to Insulin Lispro (Humalog) in Children and Adolescents With Type 1 Diabetes — Completed
• A Phase 2, Multicenter, Randomized, Double-blind, Placebo-controlled Study to Evaluate the Efficacy, Safety, and Tolerability of TAK-935 (OV935) as an Adjunctive Therapy in Pediatric Participants With Developmental and/or Epileptic Encephalopathies — Completed