Charité - Universitätsmedizin Berlin SPZ Abteilung Neuropaediatrie

Berlin 13353

2 studies enrolling now · 2 studies all time

What they study most

Muscular Atrophy, Spinal

Studies at this site

• A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy — Recruiting now
• A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy — Recruiting now