Centre de maladies rares CHNO des Quinze Vingt
Paris 75012
1 studies enrolling now · 3 studies all time
What they study most
Blindness, Deaf Blind, Eye Diseases, Eye Diseases, Hereditary, Eye Disorders Congenital, Leber Congenital Amaurosis, Leber Congenital Amaurosis 10, Neurologic Manifestations, Neurological Manifestations, Retinal Disease, Retinitis Pigmentosa (RP), Sensation Disorders
Studies at this site
- Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION) — Recruiting now
- Study to Evaluate Ultevursen in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene — Running, not enrolling
- A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE) — Running, not enrolling