Boston Children's Hospital/Massachusetts General Hospital

Boston, Massachusetts 02215

0 studies enrolling now · 4 studies all time

What they study most

Adrenoleukodystrophy (ALD), Cerebral Adrenoleukodystrophy (CALD), X-Linked Adrenoleukodystrophy (X-ALD)

Studies at this site

• Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product — Running, not enrolling
• A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD) — Completed
• A Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD) — Completed
• Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD) — Stopped early