Benioff Children's Hospital
Oakland, California 94158
0 studies enrolling now ยท 1 studies all time
What they study most
Beta-Galactosidase-1 (GLB1) Deficiency, GM1 Gangliosidosis, GM1 Gangliosidosis, Type 2, GM1 Gangliosidosis, Type I
Studies at this site
- Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis โ Running, not enrolling