Bambino Gesu Hospital

Rome 165

0 studies enrolling now · 3 studies all time

What they study most

Deep Vein Thrombosis, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, Muscular Diseases, Muscular Disorders, Atrophic, Muscular Dystrophies, Muscular Dystrophy, Duchenne, Musculoskeletal Diseases, Nervous System Diseases, Neuromuscular Diseases, Venous Thromboembolism

Studies at this site

• Phase 1 Pediatric Pharmacokinetics/Pharmacodynamics (PK/PD) Study — Completed
• An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy — Stopped early
• Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) — Completed