Bambino Gesù Children's Hospital

Rome 4-00165

0 studies enrolling now · 4 studies all time

What they study most

Alagille Syndrome, Batten Disease, CLN2 Disease, Jansky-Bielschowsky Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2, Myotubular Myopathy, Relapsed/Refractory B-Cell Non-Hodgkin Lymphoma, Relapsed/Refractory B-precursor Acute Lymphoblastic Leukemia

Studies at this site

• Study Evaluating Brexucabtagene Autoleucel (KTE-X19) in Pediatric and Adolescent Participants With Relapsed/Refractory B-precursor Acute Lymphoblastic Leukemia or Relapsed/Refractory B-Cell Non-Hodgkin Lymphoma — Completed
• Efficacy and Safety of Odevixibat in Patients With Alagille Syndrome — Completed
• A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease — Completed
• Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM) — Completed