AP-HP - Hôpital Armand Trousseau

Paris 75012

2 studies enrolling now · 3 studies all time

What they study most

Friedreich Ataxia, GM1 Gangliosidosis, GM2 Gangliosidosis, Gangliosidoses, GM2, Gangliosidosis, GM1, Niemann-Pick Type C Disease

Studies at this site

• A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis — Recruiting now
• A Study to Learn More About the Effects and Long-Term Safety of Omaveloxolone (BIIB141) in Children and Teens With Friedreich's Ataxia — Recruiting now
• A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis — Running, not enrolling