AP-HP Hopital Universitaire Necker-Enfants Malades
Paris 75015
1 studies enrolling now ยท 1 studies all time
What they study most
Phosphomannomutase 2 Deficiency, Pmm2-CDG
Studies at this site
- Open-Label Extension Study to Assess GLM101 in PMM2-CDG Patients โ Enrolling by invitation