APHP-Hopital Necker Enfants malades

Paris, Île-de-France Region 75015

0 studies enrolling now · 1 studies all time

What they study most

Hemophilia A

Studies at this site

• Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle" — Running, not enrolling