AP-HP Hopital Necker-Enfants Malades

Paris 75015

1 studies enrolling now · 4 studies all time

What they study most

Angelman Syndrome, HSV Infection, PMM2-CDG, Phosphomannomutase 2 Deficiency

Studies at this site

• Long-term Extension of GTX-102 in Angelman Syndrome — Enrolling by invitation
• Trial on Efficacy and Safety of Pritelivir Tablets for Treatment of Acyclovir-resistant Mucocutaneous HSV (Herpes Simplex Virus) Infections in Immunocompromised Subjects — Completed
• A Study to Assess the Efficacy and Safety of Weekly Doses of GLM101 in Participants With PMM2-CDG — Running, not enrolling
• A Study of the Safety and Tolerability of GTX-102 in Children With Angelman Syndrome — Completed